Pig models for Duchenne muscular dystrophy – from disease mechanisms to validation of new diagnostic and therapeutic concepts - Neuromuscular Disorders
Consensus on the diagnosis, treatment and follow-up of patients with Duchenne muscular dystrophy | Neurología (English Edition)
Peak functional ability and age at loss of ambulation in Duchenne muscular dystrophy - Zambon - 2022 - Developmental Medicine & Child Neurology - Wiley Online Library
Cardiovascular Disease in Duchenne Muscular Dystrophy: Overview and Insight Into Novel Therapeutic Targets - ScienceDirect
Drug Discovery of Therapies for Duchenne Muscular Dystrophy - SLAS Discovery
Pig models for Duchenne muscular dystrophy – from disease mechanisms to validation of new diagnostic and therapeutic concepts - ScienceDirect
BMI-z scores of boys with Duchenne muscular dystrophy already begin to increase before losing ambulation: a longitudinal exploration of BMI, corticosteroids and caloric intake - Neuromuscular Disorders
PDF) Cost-Effectiveness Analysis of Diagnosis of Duchenne/Becker Muscular Dystrophy in Colombia
Consensus on the diagnosis, treatment and follow-up of patients with Duchenne muscular dystrophy | Neurología (English Edition)
Muscle membrane integrity in Duchenne muscular dystrophy: recent advances in copolymer-based muscle membrane stabilizers | Skeletal Muscle | Full Text
PDF) Deflazacort vs prednisone/prednisolone for maintaining motor function and delaying loss of ambulation: A post hoc analysis from the ACT DMD trial
Progressive muscle proteome changes in a clinically relevant pig model of Duchenne muscular dystrophy | Scientific Reports
Vicious cycle of postural instability that leads to loss of ambulation... | Download Scientific Diagram
CRISPR applications for Duchenne muscular dystrophy: From animal models to potential therapies - Chey - WIREs Mechanisms of Disease - Wiley Online Library
Prognostic indicators of disease progression in Duchenne muscular dystrophy: A literature review and evidence synthesis | PLOS ONE
Clinical characteristics of DMD. a Muscular involvement in the DMD... | Download Scientific Diagram
PDF) Characterizing health state utilities associated with Duchenne muscular dystrophy: a systematic review
PDF) Genotype characterization and delayed loss of ambulation by glucocorticoids in a large cohort of patients with Duchenne muscular dystrophy
PDF) Comparison of Long-term Ambulatory Function in Patients with Duchenne Muscular Dystrophy Treated with Eteplirsen and Matched Natural History Controls
Nutrients | Free Full-Text | Metabogenic and Nutriceutical Approaches to Address Energy Dysregulation and Skeletal Muscle Wasting in Duchenne Muscular Dystrophy | HTML
Viltolarsen in Japanese Duchenne muscular dystrophy patients: A phase 1/2 study - Komaki - 2020 - Annals of Clinical and Translational Neurology - Wiley Online Library
Genes | Free Full-Text | Current Outline of Exon Skipping Trials in Duchenne Muscular Dystrophy | HTML
Frontiers | Adeno-Associated Virus (AAV)-Mediated Gene Therapy for Duchenne Muscular Dystrophy: The Issue of Transgene Persistence
New variants, challenges and pitfalls in DMD genotyping: implications in diagnosis, prognosis and therapy | Journal of Human Genetics
Peak functional ability and age at loss of ambulation in Duchenne muscular dystrophy - Zambon - 2022 - Developmental Medicine & Child Neurology - Wiley Online Library
