ΔF508 - an overview | ScienceDirect Topics
Rescue of ΔF508-CFTR Trafficking via a GRASP-Dependent Unconventional Secretion Pathway: Cell
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library
Highly Efficient Gene Editing of Cystic Fibrosis Patient-Derived Airway Basal Cells Results in Functional CFTR Correction: Molecular Therapy
Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect
Generation and characterization of a ~F508 cystic fibrosis mouse model
iPSC-Derived Intestinal Organoids from Cystic Fibrosis Patients Acquire CFTR Activity upon TALEN-Mediated Repair of the p.F508del Mutation: Molecular Therapy - Methods & Clinical Development
Towards next generation therapies for cystic fibrosis: Folding, function and pharmacology of CFTR - Journal of Cystic Fibrosis
IJMS | Free Full-Text | Unravelling the Regions of Mutant F508del-CFTR More Susceptible to the Action of Four Cystic Fibrosis Correctors | HTML
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library
PDF) Generation and characterization of a ΔF508 cystic fibrosis mouse model
Genes | Free Full-Text | Cystic Fibrosis Gene Therapy: Looking Back, Looking Forward | HTML
The ΔF508 Mutation Causes CFTR Misprocessing and Cystic Fibrosis–Like Disease in Pigs | Science Translational Medicine
Chemically modified hCFTR mRNAs recuperate lung function in a mouse model of cystic fibrosis | Scientific Reports
Frontiers | On the Corner of Models and Cure: Gene Editing in Cystic Fibrosis
Generation and characterization of a ~F508 cystic fibrosis mouse model
Frontiers | Adapting Proteostasis and Autophagy for Controlling the Pathogenesis of Cystic Fibrosis Lung Disease
Animal models of cystic fibrosis - Journal of Cystic Fibrosis
Generation and characterization of a ~F508 cystic fibrosis mouse model
Cystic Fibrosis Mouse Models
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library
Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing - The American Journal of Pathology
A mouse model for the cystic fibrosis delta F508 mutation. - Abstract - Europe PMC
In vivo correction of cystic fibrosis mediated by PNA nanoparticles | Science Advances
